Innovative Approaches to Gene Therapy
Watch this expert-led session to explore the latest trends and insights in gene therapy, including how to model immunosuppressive regimens, key study-design considerations, and the importance of age categories in nonhuman primate research.
A growing number of gene therapy products have progressed from preclinical studies to clinical development. Delivery methods in animals or humans generally fall into two categories: viral vectors—modified viruses that carry genetic material—and nonviral vectors, such as lipids, metals, or polymers. Each method presents distinct challenges and opportunities.
This presentation will explore these challenges and highlight innovative solutions using the nonhuman primate as the animal model. Case studies will be shared, covering both in-life studies and molecular biology assessments of germline cells to evaluate potential integration of gene therapy products.
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Related resources you may be interested in:
• Scientific Journal: Nonclinical Studies in Cell and Gene Therapy
• Scientific Poster: Germline Integration Assessment in Preclinical Gene Therapy Studies
• Webpage: Cell and Gene Therapy Development
Altasciences transforms the traditional outsourcing paradigm by simplifying and streamlining drug development solutions, whether for a single study or multiple programs, to offer an integrated/synchronized approach to CRO and CDMO services from lead candidate selection to clinical proof of concept, and beyond.
Julius Clinical
Rezon Bio
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